The Patient Experience
Nicholas’ Story: Empowerment Through Clinical Trials
Nicholas participated in clinical trials to advance research on sickle cell disease, including studies on exercise and lung function. While these trials did not directly improve his health, they contributed valuable insights into managing sickle cell disease complications. His positive experience underscores the importance of patient engagement in research.
Personal Accounts of FSCDR Patients:
“Dr. Blyden and staff strive to provide excellence in healthcare. I have never been disappointed with his treatment plan for me. I especially like that he allows me to have an active role in my care and treatment.”
– Kellyn G.
Supporting Data: Patient involvement in clinical trials is crucial for advancing therapies and understanding disease mechanisms.
Myth vs. Fact
Myth: Only bone marrow transplants from matched donors can cure sickle cell disease.
Fact: Gene therapy and expanded stem cell transplant options, such as cord blood and haploidentical transplants, are making curative therapies accessible to more patients, even those without a matched donor
Resource: Gene therapy for sickle cell disease: moving from the bench to the bedside